genetic engineering

Viewing posts tagged genetic engineering

Promise of Gene Therapy Being Realized?

Gene therapy has finally made it over the hump. After decades of research and some devastating setbacks, major technical hurdles have been overcome, opening up the long-anticipated promise of this field. A new approval has buoyed interest, pipelines are bubbling with new candidates and big investments are being made.

News about promising gene therapies in the clinic is sprouting up all the time. Scientific challenges remain considerable, though, and pricing will clearly be one of the biggest hurdles for gene therapies going forward.

“Today’s challenges are all around building a viable business model”

— Geoff MacKay, President and CEO of AvroBio

For the complete article at BioPharma Dive, click here.

BioPharma Dive Logo

Exciting BioPharma News

CAR-T Advances in Cancer Fight

Doctors in London say they have cured two babies of leukemia in the world’s first attempt to treat cancer with genetically engineered immune cells from a donor.

Treatments using engineered T-cells, commonly known as CAR-T, are new and not yet sold commercially. But they have shown stunning success against blood cancers. In studies so far by Novartis and Juno, about half of patients are permanently cured after receiving altered versions of their own blood cells.

Check out the entire article at MIT Technology Review.